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Official PDF TranslationActa Biochimica et Biophysica Sinica

A novel method to increase transgene expression and the stability of gene therapy-associated episomal vectors

Authors: Xi Zhang; Rui Liu; Zimeng Han; Zihan Guo; Mengying Ji; Wen Wang; Yanlong Jia; Tianyun Wang; Xiaoyin Wang

DOI: 10.3724/abbs.2025104Status: Verified Translated Edition
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Key Findings in This Report

• SAF-A expression level is positively correlated with transgene expression in episomal vectors, as demonstrated by correlation analysis and knockdown/overexpression experiments. • Knockdown of SAF-A via shRNA significantly reduces eGFP expression, while overexpression of SAF-A enhances transgene expression by over 2-fold, indicating a direct regulatory role. • The 375 bp MAR characteristic sequence in pEMEα retains functional interaction with SAF-A, supporting its use in compact episomal vectors for gene therapy. • This study provides a novel strategy to boost transgene expression and stability in non-viral episomal vectors by modulating SAF-A levels, with potential to improve gene therapy efficacy.